What is it like to be a part of patient engagement in early access? To understand the real-life impact of patient group engagement, we’ve spoken with different stakeholders involved in the process.
A patient group perspective
To understand some of the human impact, both on those involved in the engagement itself and also on the community in general, read this thought-provoking article from Nicole Gusset, President of SMA Europe and mother to a child with SMA.
Clinigen, industry and patient group perspectives
For a three-way view on patient group engagement, read this collaborative article with perspectives from a pharma company in rare diseases, Clinigen as an expert partner, and patient groups themselves.
A healthcare professional’s perspective
Dr Joe Brierley, Consultant Intensivist at Great Ormond Street Hospital and member of the Bioethics Advisory Group, speaks about the challenges he faces in paediatrics when it comes to the COVID-19 pandemic and early access.
Job Number: UK-CPL-0-003 and Date of Preparation: September 2021